European Reference Networks (ERN) have started this month! Check out this nice video on European Reference Networks for rare and complex diseases. As a reminder Rett syndrome is in the ERN called ITHACA, which stands for Intellectual disability, TeleHealth And Congenital Anomalies http://europa.eu/!Dc93bF
European Reference Networks (ERN) have started this month!
Check out this nice video on European Reference Networks for rare and complex diseases.
As a reminder Rett syndrome is in the ERN called ITHACA, which stands for
Intellectual disability, TeleHealth And Congenital Anomalies
Neurogene has announced the successful completion of enrollment in the EMBOLDEN trial of NGN-401, an investigational gene therapy for Rett syndrome. The…
rettX is the pan-European, patient-led Rett syndrome registry led by Rett Syndrome Europe, presented at ECRD 2026. Learn what it is and…
A multi-country caregiver study presented by Rett Syndrome Europe at ECRD 2026 reveals consistent unmet needs and fragmented care across Europe.