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A hopeful milestone for the Rett community in Europe
Rett Syndrome Europe welcomes the positive CHMP opinion for Daybu (trofinetide), a meaningful milestone for families affected by Rett syndrome across Europe.
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Taysha Reports Progress on TSHA-102 Gene Therapy for Rett Syndrome
Taysha Gene Therapies has shared positive longer-term interim data from its investigational gene therapy TSHA-102, with dosing now complete in the pivotal…
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Hopeful Progress: Gene Therapy Trial for Rett Syndrome Completes Enrollment
Neurogene has announced the successful completion of enrollment in the EMBOLDEN trial of NGN-401, an investigational gene therapy for Rett syndrome. The…