Many thanks to Future Rare Diseases for sharing this publication with us. You can read the full paper here.
Many thanks to Future Rare Diseases for sharing this publication with us. You can read the full paper here.
On 6–8 November 2026, Rett Forum will bring clinicians, researchers, patient organisations and industry partners together in Madrid to lay the foundations…
Rett Syndrome Europe welcomes the positive CHMP opinion for Daybu (trofinetide), a meaningful milestone for families affected by Rett syndrome across Europe.
Taysha Gene Therapies has shared positive longer-term interim data from its investigational gene therapy TSHA-102, with dosing now complete in the pivotal…