
Congratulations to David and colleagues for getting their first newsletter out in German, English and French! We look forward to hearing more about your work and will support your endeavours as much as we can!
Congratulations to David and colleagues for getting their first newsletter out in German, English and French! We look forward to hearing more about your work and will support your endeavours as much as we can!

Congratulations to David and colleagues for getting their first newsletter out in German, English and French! We look forward to hearing more about your work and will support your endeavours as much as we can!

Rett Syndrome Europe welcomes the positive CHMP opinion for Daybu (trofinetide), a meaningful milestone for families affected by Rett syndrome across Europe.

Taysha Gene Therapies has shared positive longer-term interim data from its investigational gene therapy TSHA-102, with dosing now complete in the pivotal…

Neurogene has announced the successful completion of enrollment in the EMBOLDEN trial of NGN-401, an investigational gene therapy for Rett syndrome. The…