Good news from Neurogene as they progress their gene therapy trial to the next stages. You can read their letter to the community here.
Good news from Neurogene as they progress their gene therapy trial to the next stages. You can read their letter to the community here.
Neurogene has announced the successful completion of enrollment in the EMBOLDEN trial of NGN-401, an investigational gene therapy for Rett syndrome. The…
rettX is the pan-European, patient-led Rett syndrome registry led by Rett Syndrome Europe, presented at ECRD 2026. Learn what it is and…
A multi-country caregiver study presented by Rett Syndrome Europe at ECRD 2026 reveals consistent unmet needs and fragmented care across Europe.