In the latest update published today we learn that there have been no serious adverse effects from the treatment in both the adult and paediatric trials so far. Both groups are reporting improvements in seizures, motor skills, communication/socialisation and autonomic dysfunction from parent carers and clinicians view points.
A further update will be shared later this year about the patients who receive the higher dose of the gene therapy. You can read the full letter to the community below.
Latest Update from Taysha